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\u5173\u4e8e\u57fa\u56e0\u7597\u6cd5<\/h2>\n

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\u7f55\u89c1\u75c5\u548c\u6162\u6027\u75c5\u57fa\u56e0\u7597\u6cd5\u7b80\u4ecb<\/h3>\n

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\u4e86\u89e3\u57fa\u56e0\u7597\u6cd5<\/h3>\n

[\/vc_column_text]

<\/div>[vc_column_text]\u57fa\u56e0\u7597\u6cd5\u901a\u8fc7\u5f15\u5165\u3001\u79fb\u9664\u6216\u6539\u53d8\u60a3\u8005\u7ec6\u80de\u5185\u7684\u9057\u4f20\u7269\u8d28\u6765\u53d1\u6325\u4f5c\u7528\u3002\u4e3b\u8981\u65b9\u6cd5\u5305\u62ec\u7528\u5065\u5eb7\u7684\u62f7\u8d1d\u66ff\u6362\u6709\u95ee\u9898\u7684\u57fa\u56e0\u3001\u4f7f\u529f\u80fd\u5931\u5e38\u7684\u57fa\u56e0\u5931\u6d3b\uff0c\u6216\u5c06\u65b0\u7684\u6216\u7ecf\u8fc7\u4fee\u9970\u7684\u57fa\u56e0\u5bfc\u5165\u4f53\u5185\u4ee5\u5e2e\u52a9\u6cbb\u7597\u75be\u75c5\u3002\u8fd9\u4e9b\u6280\u672f\u5229\u7528\u8f7d\u4f53\uff08\u901a\u5e38\u662f\u75c5\u6bd2\uff09\u8fdb\u884c\u8bbe\u8ba1\uff0c\u4ee5\u5b89\u5168\u5730\u5c06\u9057\u4f20\u7269\u8d28\u5bfc\u5165\u60a3\u8005\u7ec6\u80de\u3002 [\/vc_column_text][\/vc_column][\/vc_row][vc_row bottom_padding=”40″][vc_column width=”2\/3″][vc_column_text]<\/p>\n

\u5bf9\u7f55\u89c1\u75c5\u7684\u5f71\u54cd<\/h3>\n

[\/vc_column_text]

<\/div>[vc_column_text]\u7f55\u89c1\u75c5\u901a\u5e38\u88ab\u79f0\u4e3a “\u5b64\u513f\u75c5”\uff0c\u5f71\u54cd\u7740\u5168\u7403\u7ea6 4 \u4ebf\u4eba\u3002\u76ee\u524d\u5df2\u786e\u5b9a\u7684\u7f55\u89c1\u75c5\u6709 7000 \u591a\u79cd\uff0c\u4f46\u5176\u4e2d\u7ea6 95% \u7684\u75be\u75c5\u76ee\u524d\u8fd8\u6ca1\u6709\u83b7\u5f97\u6279\u51c6\u7684\u6cbb\u7597\u65b9\u6cd5\u3002\u867d\u7136\u7f55\u89c1\uff0c\u4f46\u8fd9\u4e9b\u75be\u75c5\u4f1a\u5bfc\u81f4\u4e25\u91cd\u7684\u5065\u5eb7\u5e76\u53d1\u75c7\uff0c\u5e76\u5927\u5927\u964d\u4f4e\u60a3\u8005\u7684\u751f\u6d3b\u8d28\u91cf\u3002\u76ee\u524d\u9488\u5bf9\u7f55\u89c1\u75c5\u7684\u4f20\u7edf\u6cbb\u7597\u65b9\u6cd5\u975e\u5e38\u6709\u9650\uff0c\u901a\u5e38\u53ea\u80fd\u7f13\u89e3\u75c7\u72b6\uff0c\u800c\u4e0d\u80fd\u4ece\u6839\u672c\u4e0a\u89e3\u51b3\u9057\u4f20\u75c5\u56e0\u3002\u57fa\u56e0\u7597\u6cd5\u76f4\u63a5\u9488\u5bf9\u57fa\u56e0\u7f3a\u9677\uff0c\u4e3a\u60a3\u8005\u5e26\u6765\u4e86\u5e0c\u671b\uff0c\u4e00\u6b21\u6cbb\u7597\u5c31\u6709\u53ef\u80fd\u7ec8\u751f\u6cbb\u6108\u3002\u6cbb\u7597\u810a\u9ad3\u6027\u808c\u840e\u7f29\u75c7\uff08SMA\uff09\u548c\u67d0\u4e9b\u9057\u4f20\u6027\u89c6\u7f51\u819c\u75be\u75c5\uff08Rep65 LCA\uff09\u7b49\u6210\u529f\u6848\u4f8b\u5f3a\u8c03\u4e86\u57fa\u56e0\u7597\u6cd5\u5bf9\u7f55\u89c1\u9057\u4f20\u75be\u75c5\u60a3\u8005\u7684\u6df1\u8fdc\u5f71\u54cd\u3002\u901a\u8fc7\u4ece\u6839\u6e90\u4e0a\u89e3\u51b3\u95ee\u9898\uff0c\u57fa\u56e0\u7597\u6cd5\u6709\u671b\u6539\u53d8\u6570\u767e\u4e07\u7f79\u60a3\u8fd9\u4e9b\u4f7f\u4eba\u8870\u5f31\u7684\u75be\u75c5\u7684\u60a3\u8005\u7684\u751f\u6d3b\uff0c\u4e3a\u4ed6\u4eec\u5e26\u6765\u4e00\u4e2a\u5145\u6ee1\u5e0c\u671b\u548c\u53ef\u80fd\u6027\u7684\u65b0\u65f6\u4ee3\u3002 <\/span>[\/vc_column_text][\/vc_column][vc_column el_class=”mobile-img” column_center=”true” width=”1\/3″]
\"\"<\/div>[\/vc_column][\/vc_row][vc_row bottom_padding=”50″ class=”mobile-reverse”][vc_column el_class=”mobile-img” column_center=”true” width=”1\/3″]
\"\"<\/div>[\/vc_column][vc_column width=”2\/3″][vc_column_text]<\/p>\n

\u5728\u6162\u6027\u75be\u75c5\u4e2d\u7684\u5e94\u7528<\/h3>\n

[\/vc_column_text]

<\/div>[vc_column_text]\u6162\u6027\u75be\u75c5\uff0c\u5982\u6e7f\u6027\u8001\u5e74\u6027\u9ec4\u6591\u53d8\u6027\uff08\u6e7f\u6027 AMD\uff09\u3001\u795e\u7ecf\u9000\u884c\u6027\u75be\u75c5\u3001\u5fc3\u810f\u75c5\u3001\u7cd6\u5c3f\u75c5\u548c\u67d0\u4e9b\u764c\u75c7\uff0c\u7531\u4e8e\u5176\u957f\u671f\u6027\u548c\u590d\u6742\u7684\u75c5\u56e0\uff0c\u4f46\u5176\u53d1\u75c5\u673a\u5236\u5df2\u5f97\u5230\u9a8c\u8bc1\uff0c\u56e0\u6b64\u7ed9\u6cbb\u7597\u5e26\u6765\u4e86\u5de8\u5927\u6311\u6218\u3002\u867d\u7136\u57fa\u56e0\u7597\u6cd5\u5728\u6cbb\u7597\u6162\u6027\u75be\u75c5\u65b9\u9762\u7684\u4f5c\u7528\u4ecd\u5728\u4e0d\u65ad\u663e\u73b0\uff0c\u4f46\u5176\u6f5c\u529b\u5de8\u5927\u3002\u901a\u8fc7\u5728\u5206\u5b50\u6c34\u5e73\u4e0a\u89e3\u51b3\u9057\u4f20\u503e\u5411\u548c\u6539\u53d8\u75be\u75c5\u9014\u5f84\uff0c\u57fa\u56e0\u7597\u6cd5\u53ef\u4ee5\u5f7b\u5e95\u6539\u53d8\u6162\u6027\u75c5\u7684\u6cbb\u7597\u3002\u4f8b\u5982\uff0c\u6700\u8fd1\u5f00\u53d1\u7684 CRISPR-Cas9 \u7b49\u57fa\u56e0\u7f16\u8f91\u6280\u672f\u6b63\u88ab\u7528\u4e8e\u7ea0\u6b63\u5bfc\u81f4\u56ca\u6027\u7ea4\u7ef4\u5316\u548c\u9570\u72b6\u7ec6\u80de\u6027\u8d2b\u8840\u7b49\u75be\u75c5\u7684\u57fa\u56e0\u7a81\u53d8\uff0c\u4e3a\u6301\u7eed\u7f13\u89e3\u75c5\u60c5\u548c\u63d0\u9ad8\u751f\u6d3b\u8d28\u91cf\u63d0\u4f9b\u4e86\u53ef\u80fd\u3002\u6b64\u5916\uff0c\u5c06\u57fa\u56e0\u7597\u6cd5\u5e94\u7528\u4e8e\u795e\u7ecf\u9000\u884c\u6027\u75be\u75c5\u7684\u7814\u7a76\u4e5f\u5728\u4e0d\u65ad\u63a8\u8fdb\uff0c\u6709\u53ef\u80fd\u963b\u6b62\u6216\u9006\u8f6c\u5e15\u91d1\u68ee\u6c0f\u75c7\u548c\u963f\u5c14\u8328\u6d77\u9ed8\u6c0f\u75c7\u7b49\u75be\u75c5\u7684\u53d1\u5c55\u3002\u8fd9\u4e9b\u8fdb\u5c55\u51f8\u663e\u4e86\u57fa\u56e0\u7597\u6cd5\u7684\u591a\u529f\u80fd\u6027\uff0c\u4ee5\u53ca\u5b83\u4e0d\u4ec5\u80fd\u63a7\u5236\u800c\u4e14\u6709\u53ef\u80fd\u6cbb\u6108\u6162\u6027\u75be\u75c5\u7684\u80fd\u529b\uff0c\u4e3a\u533b\u7597\u65b0\u65f6\u4ee3\u7684\u5230\u6765\u94fa\u5e73\u4e86\u9053\u8def\u3002 [\/vc_column_text][\/vc_column][\/vc_row][vc_row bottom_padding=”40″][vc_column width=”2\/3″][vc_column_text]<\/p>\n

\u6311\u6218\u4e0e\u672a\u6765\u65b9\u5411<\/h3>\n

[\/vc_column_text]

<\/div>[vc_column_text]\u5c3d\u7ba1\u57fa\u56e0\u7597\u6cd5\u524d\u666f\u5e7f\u9614\uff0c\u4f46\u4e5f\u9762\u4e34\u7740\u4e00\u4e9b\u6311\u6218\uff0c\u5305\u62ec\u6210\u529f\u8f93\u9001\u3001\u5bf9\u6cbb\u7597\u7684\u514d\u75ab\u53cd\u5e94\u4ee5\u53ca\u4f26\u7406\u65b9\u9762\u7684\u8003\u8651\u3002\u786e\u4fdd\u957f\u671f\u7597\u6548\u548c\u5b89\u5168\u6027\u4ecd\u662f\u5f53\u524d\u7814\u7a76\u7684\u91cd\u70b9\u3002\u968f\u7740\u79d1\u5b66\u5bb6\u548c\u4e34\u5e8a\u533b\u751f\u4e0d\u65ad\u5b8c\u5584\u8fd9\u4e9b\u6280\u672f\uff0c\u76d1\u7ba1\u673a\u6784\u3001\u7814\u7a76\u4eba\u5458\u548c\u60a3\u8005\u6743\u76ca\u56e2\u4f53\u4e4b\u95f4\u7684\u5408\u4f5c\u5bf9\u4e8e\u5e94\u5bf9\u8fd9\u4e9b\u6311\u6218\u5e76\u4e3a\u66f4\u591a\u60a3\u8005\u63d0\u4f9b\u57fa\u56e0\u6cbb\u7597\u81f3\u5173\u91cd\u8981\u3002 [\/vc_column_text][\/vc_column][vc_column el_class=”mobile-img” column_center=”true” width=”1\/3″]
\"\"<\/div>[\/vc_column][\/vc_row][vc_row top_padding=”40″ bottom_padding=”80″][vc_column el_class=”rounded-box” bg_color=”#DEEAF8″ column_padding=”custom-padding” column_custompadding=”40px” width=”1\/1″][vc_row_inner][vc_column_inner el_class=”mobile-img” width=”1\/6″]
\"\"<\/div>[\/vc_column_inner][vc_column_inner width=”5\/6″][vc_column_text]<\/p>\n

\u57fa\u56e0\u7597\u6cd5\u7ad9\u5728\u533b\u5b66\u65b0\u65f6\u4ee3\u7684\u524d\u6cbf\uff0c\u6709\u53ef\u80fd\u6539\u53d8\u7f55\u89c1\u75c5\u548c\u6162\u6027\u75c5\u7684\u6cbb\u7597\u683c\u5c40\u3002\u57fa\u56e0\u7597\u6cd5\u6709\u53ef\u80fd\u5c06\u4f9d\u8d56\u6301\u7eed\u7528\u836f\u548c\u9891\u7e41\u53bb\u533b\u9662\u5c31\u8bca\u7684\u75c5\u4eba\u8f6c\u53d8\u4e3a\u4e0d\u518d\u9700\u8981\u6301\u7eed\u6cbb\u7597\u7684\u4e2a\u4f53\uff0c\u8ba9\u4ed6\u4eec\u8fc7\u4e0a\u6b63\u5e38\u3001\u5065\u5eb7\u7684\u751f\u6d3b\u3002\u901a\u8fc7\u89e3\u51b3\u8fd9\u4e9b\u75be\u75c5\u7684\u9057\u4f20\u57fa\u7840\uff0c\u57fa\u56e0\u7597\u6cd5\u4e0d\u4ec5\u5e26\u6765\u4e86\u6cbb\u6108\u7684\u5e0c\u671b\uff0c\u8fd8\u4e3a\u4e2a\u6027\u5316\u548c\u7cbe\u51c6\u533b\u7597\u5f00\u8f9f\u4e86\u65b0\u9014\u5f84\u3002\u968f\u7740\u7814\u7a76\u7684\u4e0d\u65ad\u6df1\u5165\uff0c\u57fa\u56e0\u7597\u6cd5\u7684\u6301\u7eed\u53d1\u5c55\u4e3a\u5168\u4e16\u754c\u65e0\u6570\u4eba\u5e26\u6765\u4e86\u5e0c\u671b\uff0c\u6539\u53d8\u4e86\u4eba\u4eec\u7684\u751f\u6d3b\uff0c\u91cd\u65b0\u5b9a\u4e49\u4e86\u533b\u7597\u4fdd\u5065\u7684\u53ef\u80fd\u6027\u3002 <\/p><\/blockquote>\n

– \u848b\u7acb\u65b0\uff0c\u9996\u5e2d\u6267\u884c\u5b98<\/p>\n

[\/vc_column_text][\/vc_column_inner][\/vc_row_inner][\/vc_column][\/vc_row][vc_row type=”full_width_section” class=”wave-section-divider”][vc_column width=”1\/1″]

\"\"<\/div>[\/vc_column][\/vc_row][\/vc_section][vc_section full_width=”stretch_row” css=”.vc_custom_1726698714977{background-color: #28517f !important;}” el_class=”light-h-tag”][vc_row text_color=”light” top_padding=”60″ bottom_padding=”30″][vc_column width=”1\/1″][vc_column_text]<\/p>\n

\u5148\u8fdb\u7684cGMP<\/span>\u751f\u4ea7\u57fa\u5730<\/h2>\n

[\/vc_column_text][vc_separator color=”orange” align=”align_left” style=”dotted” border_width=”5″ el_width=”10″ css=”.vc_custom_1725989412357{margin-top: 13px !important;margin-bottom: 20px !important;}”][\/vc_column][\/vc_row][vc_row][vc_column text_align=”right” width=”1\/3″][vc_column_text]<\/p>\n

\u4eba\u624d\u6d4e\u6d4e\u3001\u7ecf\u9a8c\u4e30\u5bcc\u7684\u56e2\u961f\uff1a<\/h3>\n

[\/vc_column_text][\/vc_column][vc_column text_color=”light” width=”2\/3″][vc_column_text]\u6211\u4eec\u7684 NGGT \u56e2\u961f\u7531\u7ecf\u9a8c\u4e30\u5bcc\u7684\u4e13\u5bb6\u7ec4\u6210\uff0c\u4ed6\u4eec\u5728\u5927\u89c4\u6a21\u5236\u5907\u91cd\u7ec4\u817a\u76f8\u5173\u75c5\u6bd2 (rAAV) \u65b9\u9762\u62e5\u6709 30 \u591a\u5e74\u7684\u7ecf\u9a8c\uff0c\u5728\u4e24\u79cd\u4e0a\u5e02\u57fa\u56e0\u6cbb\u7597\u836f\u7269\u7684\u5f00\u53d1\u548c\u5546\u4e1a\u5316\u8fc7\u7a0b\u4e2d\u53d1\u6325\u4e86\u5173\u952e\u4f5c\u7528\u3002[\/vc_column_text]

<\/div>
<\/div>[\/vc_column][\/vc_row][vc_row][vc_column text_align=”right” width=”1\/3″][vc_column_text]<\/p>\n

\u9ad8\u79d1\u6280\u8bbe\u65bd\uff1a<\/h3>\n

[\/vc_column_text][\/vc_column][vc_column text_color=”light” width=”2\/3″][vc_column_text]\u6211\u4eec\u5360\u5730 90,000 \u5e73\u65b9\u82f1\u5c3a\uff0c\u62e5\u6709\u6700\u5148\u8fdb\u7684 cGMP \u8bbe\u65bd\uff0c\u53ef\u652f\u6301 rAAV \u751f\u4ea7\u7684\u6bcf\u4e2a\u9636\u6bb5\u3002\u4ece\u8d28\u7c92\u5236\u5907\u548c\u75c5\u6bd2\u8f7d\u4f53\u751f\u4ea7\u5230\u6700\u7ec8\u704c\u88c5\uff0c\u6211\u4eec\u5168\u9762\u7684\u5185\u90e8\u89e3\u51b3\u65b9\u6848\u53ef\u786e\u4fdd\u65e0\u7f1d\u3001\u9ad8\u6548\u7684\u8fd0\u8425\u3002 [\/vc_column_text]

<\/div>
<\/div>[\/vc_column][\/vc_row][vc_row][vc_column text_align=”right” width=”1\/3″][vc_column_text]<\/p>\n

\u65e0\u7f1d\u8d28\u91cf\u63a7\u5236\uff1a<\/h3>\n

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\"\"<\/div>[\/vc_column][vc_column width=”1\/4″]
\"\"<\/div>[\/vc_column][vc_column width=”1\/4″]
\"\"<\/div>[\/vc_column][vc_column width=”1\/4″]
\"\"<\/div>[\/vc_column][\/vc_row][vc_row type=”full_width_section” class=”wave-section-divider”][vc_column width=”1\/1″]
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\u4e00\u4e2a\u76ee\u6807\uff0c\u4e24\u9897\u5b50\u5f39 “\u7684\u6982\u5ff5\u662f\u57fa\u4e8e\u53cc\u529f\u80fd\u8f7d\u4f53\uff0c\u8be5\u8f7d\u4f53\u7531\u914d\u7f6e\u4e3a\u8868\u8fbe\u81f3\u5c11\u4e24\u79cd\u6d3b\u6027\u5236\u5242\u7684\u6838\u9178\u7ec4\u6210\u3002<\/h3>\n

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    \n
  • “Bullet 1 “\u901a\u8fc7\u8f7d\u4f53\u4e2d\u7684 shRNA \u6216 miRNA \u5e8f\u5217\u8868\u8fbe siRNA\uff0c\u7528\u4e8e\u6c89\u9ed8\u76ee\u6807\u57fa\u56e0\u7684\u5185\u6e90\u6027 mRNA\u3002<\/li>\n
  • “Bullet 2 “\u8868\u8fbe\u7684\u662f\u88ab\u6c89\u9ed8\u7684\u7a81\u53d8\u57fa\u56e0\u7684\u6b63\u786e\u86cb\u767d\u8d28\u7248\u672c\uff0c\u5b83\u5bf9 Bullet 1 \u7684\u6c89\u9ed8\u6d3b\u6027\u4e0d\u654f\u611f\u3002<\/li>\n<\/ul>\n

    \u6211\u4eec\u7684\u8f7d\u4f53\u65e8\u5728\u901a\u8fc7\u51cf\u5c11\u5185\u6e90\u6027\u6bd2\u6027\u7a81\u53d8\u4f53\u4ee5\u53ca\u76ee\u6807\u86cb\u767d\u7684 WT \u57fa\u56e0\u8868\u8fbe\uff0c\u540c\u65f6\u901a\u8fc7\u5f15\u5165\u76ee\u6807\u57fa\u56e0\u7684\u57fa\u56e0\u5de5\u7a0b\u62f7\u8d1d\u6765\u7ef4\u6301\u86cb\u767d\u6c34\u5e73\u548c\u6d3b\u6027\uff0c\u4ece\u800c\u5b9e\u73b0\u4f18\u5316\u6cbb\u7597\u3002\u6211\u4eec\u7684\u7f8e\u56fd\u4e13\u5229\u8fd8\u63cf\u8ff0\u4e86\u5236\u4f5c\u53cc\u529f\u80fd\u8f7d\u4f53\u7684\u65b9\u6cd5\uff0c\u4ee5\u53ca\u4f7f\u7528\u8f7d\u4f53\u6cbb\u7597\u75be\u75c5\u548c\u521b\u5efa\u52a8\u7269\u6a21\u578b\u7684\u65b9\u6cd5\u3002<\/p>\n

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    \u79d1\u5b66\u4e0e\u51fa\u7248<\/h2>\n

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[\/vc_column_text][vc_column_text]\u6162\u6027\u75be\u75c5\uff0c\u5982\u6e7f\u6027\u8001\u5e74\u6027\u9ec4\u6591\u53d8\u6027\uff08\u6e7f\u6027 AMD\uff09\u3001\u795e\u7ecf\u9000\u884c\u6027\u75be\u75c5\u3001\u5fc3\u810f\u75c5\u3001\u7cd6\u5c3f\u75c5\u548c\u67d0\u4e9b\u764c\u75c7\uff0c\u7531\u4e8e\u5176\u957f\u671f\u6027\u548c\u590d\u6742\u7684\u75c5\u56e0\uff0c\u4f46\u5176\u53d1\u75c5\u673a\u5236\u5df2\u5f97\u5230\u9a8c\u8bc1\uff0c\u56e0\u6b64\u7ed9\u6cbb\u7597\u5e26\u6765\u4e86\u5de8\u5927\u6311\u6218\u3002\u867d\u7136\u57fa\u56e0\u7597\u6cd5\u5728\u6cbb\u7597\u6162\u6027\u75be\u75c5\u65b9\u9762\u7684\u4f5c\u7528\u4ecd\u5728\u4e0d\u65ad\u663e\u73b0\uff0c\u4f46\u5176\u6f5c\u529b\u5de8\u5927\u3002\u901a\u8fc7\u5728\u5206\u5b50\u6c34\u5e73\u4e0a\u89e3\u51b3\u9057\u4f20\u503e\u5411\u548c\u6539\u53d8\u75be\u75c5\u9014\u5f84\uff0c\u57fa\u56e0\u7597\u6cd5\u53ef\u4ee5\u5f7b\u5e95\u6539\u53d8\u6162\u6027\u75c5\u7684\u6cbb\u7597\u3002\u4f8b\u5982\uff0c\u6700\u8fd1\u5f00\u53d1\u7684 CRISPR-Cas9 \u7b49\u57fa\u56e0\u7f16\u8f91\u6280\u672f\u6b63\u88ab\u7528\u4e8e\u7ea0\u6b63\u5bfc\u81f4\u56ca\u6027\u7ea4\u7ef4\u5316\u548c\u9570\u72b6\u7ec6\u80de\u6027\u8d2b\u8840\u7b49\u75be\u75c5\u7684\u57fa\u56e0\u7a81\u53d8\uff0c\u4e3a\u6301\u7eed\u7f13\u89e3\u75c5\u60c5\u548c\u63d0\u9ad8\u751f\u6d3b\u8d28\u91cf\u63d0\u4f9b\u4e86\u53ef\u80fd\u3002\u6b64\u5916\uff0c\u5c06\u57fa\u56e0\u7597\u6cd5\u5e94\u7528\u4e8e\u795e\u7ecf\u9000\u884c\u6027\u75be\u75c5\u7684\u7814\u7a76\u4e5f\u5728\u4e0d\u65ad\u63a8\u8fdb\uff0c\u6709\u53ef\u80fd\u963b\u6b62\u6216\u9006\u8f6c\u5e15\u91d1\u68ee\u6c0f\u75c7\u548c\u963f\u5c14\u8328\u6d77\u9ed8\u6c0f\u75c7\u7b49\u75be\u75c5\u7684\u53d1\u5c55\u3002\u8fd9\u4e9b\u8fdb\u5c55\u51f8\u663e\u4e86\u57fa\u56e0\u7597\u6cd5\u7684\u591a\u529f\u80fd\u6027\uff0c\u4ee5\u53ca\u5b83\u4e0d\u4ec5\u80fd\u63a7\u5236\u800c\u4e14\u6709\u53ef\u80fd\u6cbb\u6108\u6162\u6027\u75be\u75c5\u7684\u80fd\u529b\uff0c\u4e3a\u533b\u7597\u65b0\u65f6\u4ee3\u7684\u5230\u6765\u94fa\u5e73\u4e86\u9053\u8def\u3002 [\/vc_column_text][\/vc_column][\/vc_row][vc_row bottom_padding=”40″][vc_column width=”2\/3″][vc_column_text] \u6311\u6218\u4e0e\u672a\u6765\u65b9\u5411 [\/vc_column_text][vc_column_text]\u5c3d\u7ba1\u57fa\u56e0\u7597\u6cd5\u524d\u666f\u5e7f\u9614\uff0c\u4f46\u4e5f\u9762\u4e34\u7740\u4e00\u4e9b\u6311\u6218\uff0c\u5305\u62ec\u6210\u529f\u8f93\u9001\u3001\u5bf9\u6cbb\u7597\u7684\u514d\u75ab\u53cd\u5e94\u4ee5\u53ca\u4f26\u7406\u65b9\u9762\u7684\u8003\u8651\u3002\u786e\u4fdd\u957f\u671f\u7597\u6548\u548c\u5b89\u5168\u6027\u4ecd\u662f\u5f53\u524d\u7814\u7a76\u7684\u91cd\u70b9\u3002\u968f\u7740\u79d1\u5b66\u5bb6\u548c\u4e34\u5e8a\u533b\u751f\u4e0d\u65ad\u5b8c\u5584\u8fd9\u4e9b\u6280\u672f\uff0c\u76d1\u7ba1\u673a\u6784\u3001\u7814\u7a76\u4eba\u5458\u548c\u60a3\u8005\u6743\u76ca\u56e2\u4f53\u4e4b\u95f4\u7684\u5408\u4f5c\u5bf9\u4e8e\u5e94\u5bf9\u8fd9\u4e9b\u6311\u6218\u5e76\u4e3a\u66f4\u591a\u60a3\u8005\u63d0\u4f9b\u57fa\u56e0\u6cbb\u7597\u81f3\u5173\u91cd\u8981\u3002 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– \u848b\u7acb\u65b0\uff0c\u9996\u5e2d\u6267\u884c\u5b98 [\/vc_column_text][\/vc_column_inner][\/vc_row_inner][\/vc_column][\/vc_row][vc_row type=”full_width_section” class=”wave-section-divider”][vc_column width=”1\/1″][\/vc_column][\/vc_row][\/vc_section][vc_section full_width=”stretch_row” css=”.vc_custom_1726698714977{background-color: #28517f !important;}” el_class=”light-h-tag”][vc_row text_color=”light” top_padding=”60″ bottom_padding=”30″][vc_column width=”1\/1″][vc_column_text] \u5148\u8fdb\u7684cGMP\u751f\u4ea7\u57fa\u5730 [\/vc_column_text][vc_separator color=”orange” align=”align_left” style=”dotted” border_width=”5″ el_width=”10″ css=”.vc_custom_1725989412357{margin-top: 13px !important;margin-bottom: 20px !important;}”][\/vc_column][\/vc_row][vc_row][vc_column text_align=”right” width=”1\/3″][vc_column_text] \u4eba\u624d\u6d4e\u6d4e\u3001\u7ecf\u9a8c\u4e30\u5bcc\u7684\u56e2\u961f\uff1a [\/vc_column_text][\/vc_column][vc_column text_color=”light” width=”2\/3″][vc_column_text]\u6211\u4eec\u7684 NGGT \u56e2\u961f\u7531\u7ecf\u9a8c\u4e30\u5bcc\u7684\u4e13\u5bb6\u7ec4\u6210\uff0c\u4ed6\u4eec\u5728\u5927\u89c4\u6a21\u5236\u5907\u91cd\u7ec4\u817a\u76f8\u5173\u75c5\u6bd2 (rAAV) \u65b9\u9762\u62e5\u6709 30 \u591a\u5e74\u7684\u7ecf\u9a8c\uff0c\u5728\u4e24\u79cd\u4e0a\u5e02\u57fa\u56e0\u6cbb\u7597\u836f\u7269\u7684\u5f00\u53d1\u548c\u5546\u4e1a\u5316\u8fc7\u7a0b\u4e2d\u53d1\u6325\u4e86\u5173\u952e\u4f5c\u7528\u3002[\/vc_column_text][\/vc_column][\/vc_row][vc_row][vc_column text_align=”right” width=”1\/3″][vc_column_text] \u9ad8\u79d1\u6280\u8bbe\u65bd\uff1a [\/vc_column_text][\/vc_column][vc_column text_color=”light” width=”2\/3″][vc_column_text]\u6211\u4eec\u5360\u5730 90,000 \u5e73\u65b9\u82f1\u5c3a\uff0c\u62e5\u6709\u6700\u5148\u8fdb\u7684 cGMP \u8bbe\u65bd\uff0c\u53ef\u652f\u6301 rAAV \u751f\u4ea7\u7684\u6bcf\u4e2a\u9636\u6bb5\u3002\u4ece\u8d28\u7c92\u5236\u5907\u548c\u75c5\u6bd2\u8f7d\u4f53\u751f\u4ea7\u5230\u6700\u7ec8\u704c\u88c5\uff0c\u6211\u4eec\u5168\u9762\u7684\u5185\u90e8\u89e3\u51b3\u65b9\u6848\u53ef\u786e\u4fdd\u65e0\u7f1d\u3001\u9ad8\u6548\u7684\u8fd0\u8425\u3002 [\/vc_column_text][\/vc_column][\/vc_row][vc_row][vc_column text_align=”right” width=”1\/3″][vc_column_text] \u65e0\u7f1d\u8d28\u91cf\u63a7\u5236\uff1a [\/vc_column_text][\/vc_column][vc_column text_color=”light” width=”2\/3″][vc_column_text]\u6211\u4eec\u901a\u8fc7\u4e00\u4f53\u5316\u8fd0\u8425\uff0c\u5c06\u8d28\u91cf\u548c\u6548\u7387\u653e\u5728\u9996\u4f4d\uff0c\u786e\u4fdd\u751f\u4ea7\u8fc7\u7a0b\u7684\u6bcf\u4e00\u6b65\u90fd\u7b26\u5408\u6700\u9ad8\u6807\u51c6\u3002[\/vc_column_text][\/vc_column][\/vc_row][vc_row bottom_padding=”60″][vc_column text_align=”right” width=”1\/3″][vc_column_text] \u76d1\u7ba1\u5353\u8d8a\uff1a [\/vc_column_text][\/vc_column][vc_column text_color=”light” 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class=”wave-section-divider”][vc_column width=”1\/1″][\/vc_column][\/vc_row][\/vc_section][vc_section full_width=”stretch_row”][vc_row top_padding=”60″ bottom_padding=”40″][vc_column el_class=”mobile-img” width=”1\/1″][vc_column_text] \u6211\u4eec\u7684\u6280\u672f [\/vc_column_text][vc_separator color=”orange” align=”align_left” style=”dotted” border_width=”5″ el_width=”10″ css=”.vc_custom_1726700090095{margin-top: 13px !important;margin-bottom: 30px !important;}”][vc_column_text] \u4e00\u4e2a\u76ee\u6807\uff0c\u4e24\u9897\u5b50\u5f39 “\u7684\u6982\u5ff5\u662f\u57fa\u4e8e\u53cc\u529f\u80fd\u8f7d\u4f53\uff0c\u8be5\u8f7d\u4f53\u7531\u914d\u7f6e\u4e3a\u8868\u8fbe\u81f3\u5c11\u4e24\u79cd\u6d3b\u6027\u5236\u5242\u7684\u6838\u9178\u7ec4\u6210\u3002 [\/vc_column_text][\/vc_column][\/vc_row][vc_row bottom_padding=”40″][vc_column el_class=”mobile-img” column_center=”true” width=”1\/2″][\/vc_column][vc_column width=”1\/2″][vc_column_text] “Bullet 1 “\u901a\u8fc7\u8f7d\u4f53\u4e2d\u7684 shRNA 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