{"id":455,"date":"2024-05-09T19:44:54","date_gmt":"2024-05-09T23:44:54","guid":{"rendered":"https:\/\/nggtbio.com\/nggt-%e7%94%9f%e7%89%a9%e6%8a%80%e6%9c%af%e5%85%ac%e5%8f%b8%e7%9a%84%e5%9f%ba%e5%9b%a0%e7%96%97%e6%b3%95-nggt001-%e8%83%bd%e6%94%b9%e5%96%84%e6%af%94%e8%92%82%e6%b0%8f%e6%99%b6%e4%bd%93%e8%90%a5\/"},"modified":"2024-05-09T19:44:54","modified_gmt":"2024-05-09T23:44:54","slug":"nggt-%e7%94%9f%e7%89%a9%e6%8a%80%e6%9c%af%e5%85%ac%e5%8f%b8%e7%9a%84%e5%9f%ba%e5%9b%a0%e7%96%97%e6%b3%95-nggt001-%e8%83%bd%e6%94%b9%e5%96%84%e6%af%94%e8%92%82%e6%b0%8f%e6%99%b6%e4%bd%93%e8%90%a5","status":"publish","type":"post","link":"https:\/\/nggtbio.com\/zh-hans\/nggt-%e7%94%9f%e7%89%a9%e6%8a%80%e6%9c%af%e5%85%ac%e5%8f%b8%e7%9a%84%e5%9f%ba%e5%9b%a0%e7%96%97%e6%b3%95-nggt001-%e8%83%bd%e6%94%b9%e5%96%84%e6%af%94%e8%92%82%e6%b0%8f%e6%99%b6%e4%bd%93%e8%90%a5\/","title":{"rendered":"NGGT \u751f\u7269\u6280\u672f\u516c\u53f8\u7684\u57fa\u56e0\u7597\u6cd5 NGGT001 \u80fd\u6539\u5584\u6bd4\u8482\u6c0f\u6676\u4f53\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u7684\u89c6\u529b"},"content":{"rendered":"<p>\u4e0b\u4e00\u4ee3\u57fa\u56e0\u6cbb\u7597\u516c\u53f8\uff08NGGT\uff09\u751f\u7269\u6280\u672f\u516c\u53f8\u7684NGGT001\u662f\u4e00\u79cd\u57fa\u4e8e\u817a\u76f8\u5173\u75c5\u6bd2\uff08AAV\uff09\u8f7d\u4f53\u7684\u57fa\u56e0\u7597\u6cd5\uff0c\u65e8\u5728\u6cbb\u7597\u6bd4\u57c3\u8482\u6676\u4f53\u6027\u89d2\u819c\u8425\u517b\u4e0d\u826f\u75c7\uff08BCD\uff09\u3002\u5728\u7814\u7a76\u8005\u53d1\u8d77\u7684\u4e24\u5730\u8bd5\u9a8c\uff08NCT06302608\uff09\u4e2d\uff0cNGGT001\u6539\u5584\u4e86\u63a5\u53d7\u6cbb\u7597\u60a3\u8005\u7684\u89c6\u529b1\u30021 \u8be5\u7814\u7a76\u7ed3\u679c\u5728 2024 \u5e74 5 \u6708 7 \u65e5\u81f3 10 \u65e5\u4e8e\u9a6c\u91cc\u5170\u5dde\u5df4\u5c14\u7684\u6469\u5e02\u4e3e\u884c\u7684\u7f8e\u56fd\u57fa\u56e0\u4e0e\u7ec6\u80de\u7597\u6cd5\u534f\u4f1a\uff08ASGCT\uff09\u7b2c 27 \u5c4a\u5e74\u4f1a\u4e0a\u4ee5\u6d77\u62a5\u5f62\u5f0f\u516c\u5e03\u3002\u5728\u63a5\u53d7\u57fa\u56e0\u6cbb\u7597\u4ea7\u54c1\u6cbb\u75979\u4e2a\u6708\u540e\uff0c\u63a5\u53d7\u8be5\u7814\u7a76\u6cbb\u7597\u7684\u53ef\u8bc4\u4f30\u60a3\u8005\u7684\u89c6\u529b\u8f83\u57fa\u7ebf\u63d0\u9ad8\u4e8612.8 \u00b1 3.7\uff08\u5e73\u5747\u503c \u00b1 SEM\uff0cn = 11\uff09\u4e2aETDRS\u5b57\u6bcd\uff0c\u76f8\u5f53\u4e8e\u5728\u65af\u5948\u4f26\u89c6\u529b\u8868\u4e0a\u63d0\u9ad8\u4e862-3\u884c\uff08P = .0026\uff09\u3002\u6b64\u5916\uff0c\u5171\u540c\u7b2c\u4e00\u4f5c\u8005\u3001\u53a6\u95e8\u5927\u5b66\u9644\u5c5e\u53a6\u95e8\u773c\u79d1\u4e2d\u5fc3\uff08Xiamen Eye Center of Xiamen University No.989\uff09\u7684\u9648\u79c0\u83ca\u53ca\u5176\u540c\u4e8b\u6307\u51fa\uff0c\u572811\u540d\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u4e2d\uff0c\u67095\u4eba\uff0846%\uff09\u7684\u89c6\u529b\u6bd4\u57fa\u7ebf\u63d0\u9ad8\u4e8615\u4e2aETDRS\u5b57\u6bcd\u4ee5\u4e0a\u3002&#8221;Chen\u53ca\u5176\u540c\u4e8b\u5728\u6d77\u62a5\u6458\u8981\u4e2d\u5199\u9053\uff1a&#8221;BCD\u662f\u7531\u7ec6\u80de\u8272\u7d20P450\uff08CYP\uff09\u5bb6\u65cf4\u4e9a\u5bb6\u65cfV\u6210\u54582\u57fa\u56e0\uff08CYP4V2\uff09\u7a81\u53d8\u5f15\u8d77\u7684\uff0c\u8be5\u57fa\u56e0\u7f16\u7801\u4e00\u79cd\u591a\u4e0d\u9971\u548c\u8102\u80aa\u9178\u7f9f\u5316\u9176\uff0c\u4e3b\u8981\u8868\u8fbe\u4e8e\u89c6\u7f51\u819c\u4e2d\u7684\u89c6\u7f51\u819c\u8272\u7d20\u4e0a\u76ae\u7ec6\u80de\u3002NGGT \u751f\u7269\u6280\u672f\u516c\u53f8\u5f00\u53d1\u4e86\u4e00\u79cd\u57fa\u4e8e rAAV2 \u7684\u8f7d\u4f53 NGGT001\uff0c\u5b83\u8868\u8fbe\u4e86\u7528\u4e8e\u6cbb\u7597 BCD \u7684\u7ecf\u8fc7\u5bc6\u7801\u5b50\u4f18\u5316\u7684\u4eba\u7c7b CYP4V2\u3002\u5728\u5b89\u5168\u6027\u65b9\u9762\uff0cNGGT001\u88ab\u8ba4\u4e3a\u8010\u53d7\u6027\u826f\u597d\u3002\u5176\u4e2d\u4e00\u540d\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u51fa\u73b0\u4e86\u4e24\u4f8b\u773c\u90e8\u6cbb\u7597\u7a81\u53d1\u4e0d\u826f\u4e8b\u4ef6\uff08TEAE\uff09\uff0c\u4e00\u4f8b\u662f\u7ed3\u819c\u6c34\u80bf\uff0c\u4e00\u4f8b\u662f\u773c\u7751\u6c34\u80bf\uff0c\u8fd9\u4e24\u4f8b\u4e0d\u826f\u4e8b\u4ef6\u5747\u57285\u5929\u5185\u7f13\u89e3\uff0c\u88ab\u8ba4\u4e3a\u4e0eNGGT001\u80af\u5b9a\u65e0\u5173\u3002\u5728\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u4e2d\u8fd8\u89c2\u5bdf\u5230\u4e86\u51e0\u4f8b\u975e\u773c\u90e8 TEAEs\u3002\u5176\u4e2d\u5305\u62ec\u4e00\u540d\u60a3\u8005\u7684\u4e24\u4f8b\u4e0a\u547c\u5438\u9053\u611f\u67d3\u3001\u53e6\u4e00\u540d\u60a3\u8005\u7684\u4e00\u4f8b\u5c0f\u817f\u9aa8\u5e94\u529b\u6027\u9aa8\u6298\u4ee5\u53ca\u53e6\u4e00\u540d\u60a3\u8005\u7684\u4e00\u4f8b\u54bd\u708e\u3002\u6240\u6709\u8fd9\u4e9b\u4e0d\u826f\u53cd\u5e94\u90fd\u5728 7 \u5929\u6216\u66f4\u77ed\u65f6\u95f4\u5185\u5f97\u5230\u7f13\u89e3\uff0c\u5e76\u88ab\u8ba4\u4e3a\u4e0e\u57fa\u56e0\u7597\u6cd5\u7edd\u5bf9\u65e0\u5173\u3002Chen\u53ca\u5176\u540c\u4e8b\u8fd8\u6307\u51fa\uff0c\u4e0e\u7528\u4e8e\u6ce8\u5c04NGGT001\u7684\u89c6\u7f51\u819c\u4e0b\u6ce8\u5c04\u7a0b\u5e8f\u6709\u5173\u7684\u4e0d\u826f\u53cd\u5e94\u5305\u62ec\u773c\u7751\u548c\u5de9\u819c\u4e0b\u6c34\u80bf\uff0c\u4f46\u8fd9\u4e9b\u4e0d\u826f\u53cd\u5e94\u7684\u4e25\u91cd\u7a0b\u5ea6\u8f83\u8f7b\uff0c\u5e76\u53ef\u81ea\u884c\u7f13\u89e3\u3002\u4ed6\u4eec\u8fd8\u6307\u51fa\uff0c\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u6ca1\u6709\u773c\u5185\u708e\u75c7\u7684\u8ff9\u8c61\u3002\u8be5\u8bd5\u9a8c\u5171\u5305\u62ec 12 \u540d\u60a3\u8005\uff0c\u5747\u4e3a\u4e9a\u88d4\uff0c\u5e74\u9f84\u5728 30 \u5c81\u81f3 60 \u5c81\u4e4b\u95f4\u3002\u5176\u4e2d\u5305\u62ec 7 \u540d\u7537\u6027\u548c 5 \u540d\u5973\u6027\uff0c\u4ed6\u4eec\u88ab\u786e\u8bca\u4e3a CYP4V2 \u7a81\u53d8\u7684 BCD \u60a3\u8005\u3002\u6cbb\u7597\u524d\uff0c\u6700\u4f73\u77eb\u6b63\u89c6\u529b\uff08BCVA\uff09\u4ece\u624b\u90e8\u8fd0\u52a8\u523020\/60\u4e0d\u7b49\u3002\u636e\u6089\uff0c\u6709 3 \u540d\u60a3\u8005\u7684\u57fa\u7ebf\u89c6\u529b\u504f\u79bb\u89c6\u529b\u8868\uff0c\u5176\u4e2d 2 \u540d\u60a3\u8005\u7684\u6700\u4f73\u77eb\u6b63\u89c6\u529b\u4e3a\u624b\u90e8\u8fd0\u52a8\u89c6\u529b\uff0c1 \u540d\u60a3\u8005\u7684\u6700\u4f73\u77eb\u6b63\u89c6\u529b\u4e3a\u6570\u624b\u6307\u89c6\u529b\u3002\u8bd5\u9a8c\u4e2d\u67096\u540d\u60a3\u8005\u63a5\u53d7\u4e86\u8f83\u4f4e\u5242\u91cf\u7684NGGT001\uff081.5&#215;1011 vg\/\u773c\uff09\uff0c6\u540d\u60a3\u8005\u63a5\u53d7\u4e86\u8f83\u9ad8\u5242\u91cf\u7684NGGT001\uff083.0&#215;1011 vg\/\u773c\uff09\u3002&#8221;BCD\u662f\u4e00\u79cd\u9057\u4f20\u6027\u89c6\u7f51\u819c\u8425\u517b\u4e0d\u826f\u75c7\uff0c\u5176\u7279\u5f81\u662f\u89c6\u7f51\u819c\u4e0a\u51fa\u73b0\u9ec4\u767d\u8272\u6676\u4f53\u548c\/\u6216\u590d\u6742\u7684\u8102\u8d28\u6c89\u79ef\uff0c\u5e76\u53ef\u80fd\u53d1\u5c55\u6210\u5931\u660e&#8230;&#8230;&#8221;\u3002\u9648\u53ca\u5176\u540c\u4e8b\u5728\u6d77\u62a5\u4e2d\u5199\u9053\uff1a1 &#8220;NGGT001\u5728\u6210\u5e74BCD\u60a3\u8005\u4e2d\u8010\u53d7\u6027\u826f\u597d\uff0c\u7b2c9\u4e2a\u6708\u65f6\u529f\u80fd\u6027\u89c6\u529b\u5f97\u5230\u6539\u5584&#8221;\u3002 <\/p>\n<p><a href=\"https:\/\/www.cgtlive.com\/conferences\/american-society-for-gene-cell-therapy-asgct-\" target=\"_blank\" rel=\"noopener\">\u5355\u51fb\u6b64\u5904\u67e5\u770b\u6709\u5173 2024 ASGCT \u5e74\u4f1a\u7684\u66f4\u591a\u62a5\u9053\u3002<\/a><\/p>\n<h4>\u4e3b\u8981\u6536\u83b7<\/h4>\n<ul>\n<li>\u4e0b\u4e00\u4ee3\u57fa\u56e0\u6cbb\u7597\u516c\u53f8\uff08NGGT\uff09\u751f\u7269\u6280\u672f\u516c\u53f8\u7684 NGGT001 \u662f\u4e00\u79cd\u57fa\u4e8e\u817a\u76f8\u5173\u75c5\u6bd2\uff08AAV\uff09\u8f7d\u4f53\u7684\u57fa\u56e0\u7597\u6cd5\uff0c\u7528\u4e8e\u6cbb\u7597\u6bd4\u57c3\u8482\u6676\u4f53\u6027\u89d2\u819c\u8425\u517b\u4e0d\u826f\u75c7\uff08BCD\uff09\uff0c\u5728\u7814\u7a76\u8005\u53d1\u8d77\u7684\u4e24\u5730\u8bd5\u9a8c\uff08NCT06302608\uff09\u4e2d\uff0c\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u89c6\u529b\u5f97\u5230\u6539\u5584\u3002<\/li>\n<li>\u5728\u63a5\u53d7\u57fa\u56e0\u6cbb\u7597\u4ea7\u54c1\u6cbb\u7597 9 \u4e2a\u6708\u540e\uff0c\u63a5\u53d7\u8be5\u7814\u7a76\u6cbb\u7597\u7684\u53ef\u8bc4\u4f30\u60a3\u8005\u7684\u89c6\u529b\u6bd4\u57fa\u7ebf\u63d0\u9ad8\u4e86 12.8 \u00b1 3.7\uff08\u5e73\u5747\u503c \u00b1 SEM\uff0cn = 11\uff09\u4e2a ETDRS \u5b57\u6bcd\uff0c\u76f8\u5f53\u4e8e\u5728\u65af\u5948\u4f26\u89c6\u529b\u8868\u4e0a\u63d0\u9ad8\u4e86 2-3 \u884c\uff08P = .0026\uff09\u3002<\/li>\n<li>\u4e0e\u7528\u4e8e\u6ce8\u5c04 NGGT001 \u7684\u89c6\u7f51\u819c\u4e0b\u6ce8\u5c04\u7a0b\u5e8f\u6709\u5173\u7684\u4e0d\u826f\u53cd\u5e94\u5305\u62ec\u773c\u7751\u548c\u5de9\u819c\u4e0b\u6c34\u80bf\uff0c\u4f46\u8fd9\u4e9b\u4e0d\u826f\u53cd\u5e94\u7684\u4e25\u91cd\u7a0b\u5ea6\u8f83\u8f7b\uff0c\u5e76\u53ef\u81ea\u884c\u7f13\u89e3\u3002\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u672a\u51fa\u73b0\u773c\u5185\u708e\u75c7\u8ff9\u8c61\u3002 <\/li>\n<\/ul>\n","protected":false},"excerpt":{"rendered":"<p>\u4e0b\u4e00\u4ee3\u57fa\u56e0\u6cbb\u7597\u516c\u53f8\uff08NGGT\uff09\u751f\u7269\u6280\u672f\u516c\u53f8\u7684NGGT001\u662f\u4e00\u79cd\u57fa\u4e8e\u817a\u76f8\u5173\u75c5\u6bd2\uff08AAV\uff09\u8f7d\u4f53\u7684\u57fa\u56e0\u7597\u6cd5\uff0c\u65e8\u5728\u6cbb\u7597\u6bd4\u57c3\u8482\u6676\u4f53\u6027\u89d2\u819c\u8425\u517b\u4e0d\u826f\u75c7\uff08BCD\uff09\u3002\u5728\u7814\u7a76\u8005\u53d1\u8d77\u7684\u4e24\u5730\u8bd5\u9a8c\uff08NCT06302608\uff09\u4e2d\uff0cNGGT001\u6539\u5584\u4e86\u63a5\u53d7\u6cbb\u7597\u60a3\u8005\u7684\u89c6\u529b1\u30021 \u8be5\u7814\u7a76\u7ed3\u679c\u5728 2024 \u5e74 5 \u6708 7 \u65e5\u81f3 10 \u65e5\u4e8e\u9a6c\u91cc\u5170\u5dde\u5df4\u5c14\u7684\u6469\u5e02\u4e3e\u884c\u7684\u7f8e\u56fd\u57fa\u56e0\u4e0e\u7ec6\u80de\u7597\u6cd5\u534f\u4f1a\uff08ASGCT\uff09\u7b2c 27 \u5c4a\u5e74\u4f1a\u4e0a\u4ee5\u6d77\u62a5\u5f62\u5f0f\u516c\u5e03\u3002\u5728\u63a5\u53d7\u57fa\u56e0\u6cbb\u7597\u4ea7\u54c1\u6cbb\u75979\u4e2a\u6708\u540e\uff0c\u63a5\u53d7\u8be5\u7814\u7a76\u6cbb\u7597\u7684\u53ef\u8bc4\u4f30\u60a3\u8005\u7684\u89c6\u529b\u8f83\u57fa\u7ebf\u63d0\u9ad8\u4e8612.8 \u00b1 3.7\uff08\u5e73\u5747\u503c \u00b1 SEM\uff0cn = 11\uff09\u4e2aETDRS\u5b57\u6bcd\uff0c\u76f8\u5f53\u4e8e\u5728\u65af\u5948\u4f26\u89c6\u529b\u8868\u4e0a\u63d0\u9ad8\u4e862-3\u884c\uff08P = .0026\uff09\u3002\u6b64\u5916\uff0c\u5171\u540c\u7b2c\u4e00\u4f5c\u8005\u3001\u53a6\u95e8\u5927\u5b66\u9644\u5c5e\u53a6\u95e8\u773c\u79d1\u4e2d\u5fc3\uff08Xiamen Eye Center of Xiamen University No.989\uff09\u7684\u9648\u79c0\u83ca\u53ca\u5176\u540c\u4e8b\u6307\u51fa\uff0c\u572811\u540d\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u4e2d\uff0c\u67095\u4eba\uff0846%\uff09\u7684\u89c6\u529b\u6bd4\u57fa\u7ebf\u63d0\u9ad8\u4e8615\u4e2aETDRS\u5b57\u6bcd\u4ee5\u4e0a\u3002&#8221;Chen\u53ca\u5176\u540c\u4e8b\u5728\u6d77\u62a5\u6458\u8981\u4e2d\u5199\u9053\uff1a&#8221;BCD\u662f\u7531\u7ec6\u80de\u8272\u7d20P450\uff08CYP\uff09\u5bb6\u65cf4\u4e9a\u5bb6\u65cfV\u6210\u54582\u57fa\u56e0\uff08CYP4V2\uff09\u7a81\u53d8\u5f15\u8d77\u7684\uff0c\u8be5\u57fa\u56e0\u7f16\u7801\u4e00\u79cd\u591a\u4e0d\u9971\u548c\u8102\u80aa\u9178\u7f9f\u5316\u9176\uff0c\u4e3b\u8981\u8868\u8fbe\u4e8e\u89c6\u7f51\u819c\u4e2d\u7684\u89c6\u7f51\u819c\u8272\u7d20\u4e0a\u76ae\u7ec6\u80de\u3002NGGT \u751f\u7269\u6280\u672f\u516c\u53f8\u5f00\u53d1\u4e86\u4e00\u79cd\u57fa\u4e8e rAAV2 \u7684\u8f7d\u4f53 NGGT001\uff0c\u5b83\u8868\u8fbe\u4e86\u7528\u4e8e\u6cbb\u7597 BCD \u7684\u7ecf\u8fc7\u5bc6\u7801\u5b50\u4f18\u5316\u7684\u4eba\u7c7b CYP4V2\u3002\u5728\u5b89\u5168\u6027\u65b9\u9762\uff0cNGGT001\u88ab\u8ba4\u4e3a\u8010\u53d7\u6027\u826f\u597d\u3002\u5176\u4e2d\u4e00\u540d\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u51fa\u73b0\u4e86\u4e24\u4f8b\u773c\u90e8\u6cbb\u7597\u7a81\u53d1\u4e0d\u826f\u4e8b\u4ef6\uff08TEAE\uff09\uff0c\u4e00\u4f8b\u662f\u7ed3\u819c\u6c34\u80bf\uff0c\u4e00\u4f8b\u662f\u773c\u7751\u6c34\u80bf\uff0c\u8fd9\u4e24\u4f8b\u4e0d\u826f\u4e8b\u4ef6\u5747\u57285\u5929\u5185\u7f13\u89e3\uff0c\u88ab\u8ba4\u4e3a\u4e0eNGGT001\u80af\u5b9a\u65e0\u5173\u3002\u5728\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u4e2d\u8fd8\u89c2\u5bdf\u5230\u4e86\u51e0\u4f8b\u975e\u773c\u90e8 TEAEs\u3002\u5176\u4e2d\u5305\u62ec\u4e00\u540d\u60a3\u8005\u7684\u4e24\u4f8b\u4e0a\u547c\u5438\u9053\u611f\u67d3\u3001\u53e6\u4e00\u540d\u60a3\u8005\u7684\u4e00\u4f8b\u5c0f\u817f\u9aa8\u5e94\u529b\u6027\u9aa8\u6298\u4ee5\u53ca\u53e6\u4e00\u540d\u60a3\u8005\u7684\u4e00\u4f8b\u54bd\u708e\u3002\u6240\u6709\u8fd9\u4e9b\u4e0d\u826f\u53cd\u5e94\u90fd\u5728 7 \u5929\u6216\u66f4\u77ed\u65f6\u95f4\u5185\u5f97\u5230\u7f13\u89e3\uff0c\u5e76\u88ab\u8ba4\u4e3a\u4e0e\u57fa\u56e0\u7597\u6cd5\u7edd\u5bf9\u65e0\u5173\u3002Chen\u53ca\u5176\u540c\u4e8b\u8fd8\u6307\u51fa\uff0c\u4e0e\u7528\u4e8e\u6ce8\u5c04NGGT001\u7684\u89c6\u7f51\u819c\u4e0b\u6ce8\u5c04\u7a0b\u5e8f\u6709\u5173\u7684\u4e0d\u826f\u53cd\u5e94\u5305\u62ec\u773c\u7751\u548c\u5de9\u819c\u4e0b\u6c34\u80bf\uff0c\u4f46\u8fd9\u4e9b\u4e0d\u826f\u53cd\u5e94\u7684\u4e25\u91cd\u7a0b\u5ea6\u8f83\u8f7b\uff0c\u5e76\u53ef\u81ea\u884c\u7f13\u89e3\u3002\u4ed6\u4eec\u8fd8\u6307\u51fa\uff0c\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u6ca1\u6709\u773c\u5185\u708e\u75c7\u7684\u8ff9\u8c61\u3002\u8be5\u8bd5\u9a8c\u5171\u5305\u62ec 12 \u540d\u60a3\u8005\uff0c\u5747\u4e3a\u4e9a\u88d4\uff0c\u5e74\u9f84\u5728 30 \u5c81\u81f3 60 \u5c81\u4e4b\u95f4\u3002\u5176\u4e2d\u5305\u62ec 7 \u540d\u7537\u6027\u548c 5 \u540d\u5973\u6027\uff0c\u4ed6\u4eec\u88ab\u786e\u8bca\u4e3a CYP4V2 \u7a81\u53d8\u7684 BCD \u60a3\u8005\u3002\u6cbb\u7597\u524d\uff0c\u6700\u4f73\u77eb\u6b63\u89c6\u529b\uff08BCVA\uff09\u4ece\u624b\u90e8\u8fd0\u52a8\u523020\/60\u4e0d\u7b49\u3002\u636e\u6089\uff0c\u6709 3 \u540d\u60a3\u8005\u7684\u57fa\u7ebf\u89c6\u529b\u504f\u79bb\u89c6\u529b\u8868\uff0c\u5176\u4e2d 2 \u540d\u60a3\u8005\u7684\u6700\u4f73\u77eb\u6b63\u89c6\u529b\u4e3a\u624b\u90e8\u8fd0\u52a8\u89c6\u529b\uff0c1 \u540d\u60a3\u8005\u7684\u6700\u4f73\u77eb\u6b63\u89c6\u529b\u4e3a\u6570\u624b\u6307\u89c6\u529b\u3002\u8bd5\u9a8c\u4e2d\u67096\u540d\u60a3\u8005\u63a5\u53d7\u4e86\u8f83\u4f4e\u5242\u91cf\u7684NGGT001\uff081.5&#215;1011 vg\/\u773c\uff09\uff0c6\u540d\u60a3\u8005\u63a5\u53d7\u4e86\u8f83\u9ad8\u5242\u91cf\u7684NGGT001\uff083.0&#215;1011 vg\/\u773c\uff09\u3002&#8221;BCD\u662f\u4e00\u79cd\u9057\u4f20\u6027\u89c6\u7f51\u819c\u8425\u517b\u4e0d\u826f\u75c7\uff0c\u5176\u7279\u5f81\u662f\u89c6\u7f51\u819c\u4e0a\u51fa\u73b0\u9ec4\u767d\u8272\u6676\u4f53\u548c\/\u6216\u590d\u6742\u7684\u8102\u8d28\u6c89\u79ef\uff0c\u5e76\u53ef\u80fd\u53d1\u5c55\u6210\u5931\u660e&#8230;&#8230;&#8221;\u3002\u9648\u53ca\u5176\u540c\u4e8b\u5728\u6d77\u62a5\u4e2d\u5199\u9053\uff1a1 &#8220;NGGT001\u5728\u6210\u5e74BCD\u60a3\u8005\u4e2d\u8010\u53d7\u6027\u826f\u597d\uff0c\u7b2c9\u4e2a\u6708\u65f6\u529f\u80fd\u6027\u89c6\u529b\u5f97\u5230\u6539\u5584&#8221;\u3002 \u5355\u51fb\u6b64\u5904\u67e5\u770b\u6709\u5173 2024 ASGCT \u5e74\u4f1a\u7684\u66f4\u591a\u62a5\u9053\u3002 \u4e3b\u8981\u6536\u83b7 \u4e0b\u4e00\u4ee3\u57fa\u56e0\u6cbb\u7597\u516c\u53f8\uff08NGGT\uff09\u751f\u7269\u6280\u672f\u516c\u53f8\u7684 NGGT001 \u662f\u4e00\u79cd\u57fa\u4e8e\u817a\u76f8\u5173\u75c5\u6bd2\uff08AAV\uff09\u8f7d\u4f53\u7684\u57fa\u56e0\u7597\u6cd5\uff0c\u7528\u4e8e\u6cbb\u7597\u6bd4\u57c3\u8482\u6676\u4f53\u6027\u89d2\u819c\u8425\u517b\u4e0d\u826f\u75c7\uff08BCD\uff09\uff0c\u5728\u7814\u7a76\u8005\u53d1\u8d77\u7684\u4e24\u5730\u8bd5\u9a8c\uff08NCT06302608\uff09\u4e2d\uff0c\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u89c6\u529b\u5f97\u5230\u6539\u5584\u3002 \u5728\u63a5\u53d7\u57fa\u56e0\u6cbb\u7597\u4ea7\u54c1\u6cbb\u7597 9 \u4e2a\u6708\u540e\uff0c\u63a5\u53d7\u8be5\u7814\u7a76\u6cbb\u7597\u7684\u53ef\u8bc4\u4f30\u60a3\u8005\u7684\u89c6\u529b\u6bd4\u57fa\u7ebf\u63d0\u9ad8\u4e86 12.8 \u00b1 3.7\uff08\u5e73\u5747\u503c \u00b1 SEM\uff0cn = 11\uff09\u4e2a ETDRS \u5b57\u6bcd\uff0c\u76f8\u5f53\u4e8e\u5728\u65af\u5948\u4f26\u89c6\u529b\u8868\u4e0a\u63d0\u9ad8\u4e86 2-3 \u884c\uff08P = .0026\uff09\u3002 \u4e0e\u7528\u4e8e\u6ce8\u5c04 NGGT001 \u7684\u89c6\u7f51\u819c\u4e0b\u6ce8\u5c04\u7a0b\u5e8f\u6709\u5173\u7684\u4e0d\u826f\u53cd\u5e94\u5305\u62ec\u773c\u7751\u548c\u5de9\u819c\u4e0b\u6c34\u80bf\uff0c\u4f46\u8fd9\u4e9b\u4e0d\u826f\u53cd\u5e94\u7684\u4e25\u91cd\u7a0b\u5ea6\u8f83\u8f7b\uff0c\u5e76\u53ef\u81ea\u884c\u7f13\u89e3\u3002\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u672a\u51fa\u73b0\u773c\u5185\u708e\u75c7\u8ff9\u8c61\u3002<\/p>\n","protected":false},"author":2,"featured_media":365,"comment_status":"closed","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"_themeisle_gutenberg_block_has_review":false,"footnotes":""},"categories":[18,17],"tags":[],"class_list":["post-455","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-18","category-17"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v23.7 - https:\/\/yoast.com\/wordpress\/plugins\/seo\/ -->\n<title>NGGT \u751f\u7269\u6280\u672f\u516c\u53f8\u7684\u57fa\u56e0\u7597\u6cd5 NGGT001 \u80fd\u6539\u5584\u6bd4\u8482\u6c0f\u6676\u4f53\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u7684\u89c6\u529b - Next Generation Gene Therapeutics<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/nggtbio.com\/nggt-\u751f\u7269\u6280\u672f\u516c\u53f8\u7684\u57fa\u56e0\u7597\u6cd5-nggt001-\u80fd\u6539\u5584\u6bd4\u8482\u6c0f\u6676\u4f53\u8425\/\" \/>\n<meta property=\"og:locale\" content=\"zh_CN\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"NGGT \u751f\u7269\u6280\u672f\u516c\u53f8\u7684\u57fa\u56e0\u7597\u6cd5 NGGT001 \u80fd\u6539\u5584\u6bd4\u8482\u6c0f\u6676\u4f53\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u7684\u89c6\u529b - Next Generation Gene Therapeutics\" \/>\n<meta property=\"og:description\" content=\"\u4e0b\u4e00\u4ee3\u57fa\u56e0\u6cbb\u7597\u516c\u53f8\uff08NGGT\uff09\u751f\u7269\u6280\u672f\u516c\u53f8\u7684NGGT001\u662f\u4e00\u79cd\u57fa\u4e8e\u817a\u76f8\u5173\u75c5\u6bd2\uff08AAV\uff09\u8f7d\u4f53\u7684\u57fa\u56e0\u7597\u6cd5\uff0c\u65e8\u5728\u6cbb\u7597\u6bd4\u57c3\u8482\u6676\u4f53\u6027\u89d2\u819c\u8425\u517b\u4e0d\u826f\u75c7\uff08BCD\uff09\u3002\u5728\u7814\u7a76\u8005\u53d1\u8d77\u7684\u4e24\u5730\u8bd5\u9a8c\uff08NCT06302608\uff09\u4e2d\uff0cNGGT001\u6539\u5584\u4e86\u63a5\u53d7\u6cbb\u7597\u60a3\u8005\u7684\u89c6\u529b1\u30021 \u8be5\u7814\u7a76\u7ed3\u679c\u5728 2024 \u5e74 5 \u6708 7 \u65e5\u81f3 10 \u65e5\u4e8e\u9a6c\u91cc\u5170\u5dde\u5df4\u5c14\u7684\u6469\u5e02\u4e3e\u884c\u7684\u7f8e\u56fd\u57fa\u56e0\u4e0e\u7ec6\u80de\u7597\u6cd5\u534f\u4f1a\uff08ASGCT\uff09\u7b2c 27 \u5c4a\u5e74\u4f1a\u4e0a\u4ee5\u6d77\u62a5\u5f62\u5f0f\u516c\u5e03\u3002\u5728\u63a5\u53d7\u57fa\u56e0\u6cbb\u7597\u4ea7\u54c1\u6cbb\u75979\u4e2a\u6708\u540e\uff0c\u63a5\u53d7\u8be5\u7814\u7a76\u6cbb\u7597\u7684\u53ef\u8bc4\u4f30\u60a3\u8005\u7684\u89c6\u529b\u8f83\u57fa\u7ebf\u63d0\u9ad8\u4e8612.8 \u00b1 3.7\uff08\u5e73\u5747\u503c \u00b1 SEM\uff0cn = 11\uff09\u4e2aETDRS\u5b57\u6bcd\uff0c\u76f8\u5f53\u4e8e\u5728\u65af\u5948\u4f26\u89c6\u529b\u8868\u4e0a\u63d0\u9ad8\u4e862-3\u884c\uff08P = .0026\uff09\u3002\u6b64\u5916\uff0c\u5171\u540c\u7b2c\u4e00\u4f5c\u8005\u3001\u53a6\u95e8\u5927\u5b66\u9644\u5c5e\u53a6\u95e8\u773c\u79d1\u4e2d\u5fc3\uff08Xiamen Eye Center of Xiamen University No.989\uff09\u7684\u9648\u79c0\u83ca\u53ca\u5176\u540c\u4e8b\u6307\u51fa\uff0c\u572811\u540d\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u4e2d\uff0c\u67095\u4eba\uff0846%\uff09\u7684\u89c6\u529b\u6bd4\u57fa\u7ebf\u63d0\u9ad8\u4e8615\u4e2aETDRS\u5b57\u6bcd\u4ee5\u4e0a\u3002&#8221;Chen\u53ca\u5176\u540c\u4e8b\u5728\u6d77\u62a5\u6458\u8981\u4e2d\u5199\u9053\uff1a&#8221;BCD\u662f\u7531\u7ec6\u80de\u8272\u7d20P450\uff08CYP\uff09\u5bb6\u65cf4\u4e9a\u5bb6\u65cfV\u6210\u54582\u57fa\u56e0\uff08CYP4V2\uff09\u7a81\u53d8\u5f15\u8d77\u7684\uff0c\u8be5\u57fa\u56e0\u7f16\u7801\u4e00\u79cd\u591a\u4e0d\u9971\u548c\u8102\u80aa\u9178\u7f9f\u5316\u9176\uff0c\u4e3b\u8981\u8868\u8fbe\u4e8e\u89c6\u7f51\u819c\u4e2d\u7684\u89c6\u7f51\u819c\u8272\u7d20\u4e0a\u76ae\u7ec6\u80de\u3002NGGT \u751f\u7269\u6280\u672f\u516c\u53f8\u5f00\u53d1\u4e86\u4e00\u79cd\u57fa\u4e8e rAAV2 \u7684\u8f7d\u4f53 NGGT001\uff0c\u5b83\u8868\u8fbe\u4e86\u7528\u4e8e\u6cbb\u7597 BCD \u7684\u7ecf\u8fc7\u5bc6\u7801\u5b50\u4f18\u5316\u7684\u4eba\u7c7b CYP4V2\u3002\u5728\u5b89\u5168\u6027\u65b9\u9762\uff0cNGGT001\u88ab\u8ba4\u4e3a\u8010\u53d7\u6027\u826f\u597d\u3002\u5176\u4e2d\u4e00\u540d\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u51fa\u73b0\u4e86\u4e24\u4f8b\u773c\u90e8\u6cbb\u7597\u7a81\u53d1\u4e0d\u826f\u4e8b\u4ef6\uff08TEAE\uff09\uff0c\u4e00\u4f8b\u662f\u7ed3\u819c\u6c34\u80bf\uff0c\u4e00\u4f8b\u662f\u773c\u7751\u6c34\u80bf\uff0c\u8fd9\u4e24\u4f8b\u4e0d\u826f\u4e8b\u4ef6\u5747\u57285\u5929\u5185\u7f13\u89e3\uff0c\u88ab\u8ba4\u4e3a\u4e0eNGGT001\u80af\u5b9a\u65e0\u5173\u3002\u5728\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u4e2d\u8fd8\u89c2\u5bdf\u5230\u4e86\u51e0\u4f8b\u975e\u773c\u90e8 TEAEs\u3002\u5176\u4e2d\u5305\u62ec\u4e00\u540d\u60a3\u8005\u7684\u4e24\u4f8b\u4e0a\u547c\u5438\u9053\u611f\u67d3\u3001\u53e6\u4e00\u540d\u60a3\u8005\u7684\u4e00\u4f8b\u5c0f\u817f\u9aa8\u5e94\u529b\u6027\u9aa8\u6298\u4ee5\u53ca\u53e6\u4e00\u540d\u60a3\u8005\u7684\u4e00\u4f8b\u54bd\u708e\u3002\u6240\u6709\u8fd9\u4e9b\u4e0d\u826f\u53cd\u5e94\u90fd\u5728 7 \u5929\u6216\u66f4\u77ed\u65f6\u95f4\u5185\u5f97\u5230\u7f13\u89e3\uff0c\u5e76\u88ab\u8ba4\u4e3a\u4e0e\u57fa\u56e0\u7597\u6cd5\u7edd\u5bf9\u65e0\u5173\u3002Chen\u53ca\u5176\u540c\u4e8b\u8fd8\u6307\u51fa\uff0c\u4e0e\u7528\u4e8e\u6ce8\u5c04NGGT001\u7684\u89c6\u7f51\u819c\u4e0b\u6ce8\u5c04\u7a0b\u5e8f\u6709\u5173\u7684\u4e0d\u826f\u53cd\u5e94\u5305\u62ec\u773c\u7751\u548c\u5de9\u819c\u4e0b\u6c34\u80bf\uff0c\u4f46\u8fd9\u4e9b\u4e0d\u826f\u53cd\u5e94\u7684\u4e25\u91cd\u7a0b\u5ea6\u8f83\u8f7b\uff0c\u5e76\u53ef\u81ea\u884c\u7f13\u89e3\u3002\u4ed6\u4eec\u8fd8\u6307\u51fa\uff0c\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u6ca1\u6709\u773c\u5185\u708e\u75c7\u7684\u8ff9\u8c61\u3002\u8be5\u8bd5\u9a8c\u5171\u5305\u62ec 12 \u540d\u60a3\u8005\uff0c\u5747\u4e3a\u4e9a\u88d4\uff0c\u5e74\u9f84\u5728 30 \u5c81\u81f3 60 \u5c81\u4e4b\u95f4\u3002\u5176\u4e2d\u5305\u62ec 7 \u540d\u7537\u6027\u548c 5 \u540d\u5973\u6027\uff0c\u4ed6\u4eec\u88ab\u786e\u8bca\u4e3a CYP4V2 \u7a81\u53d8\u7684 BCD \u60a3\u8005\u3002\u6cbb\u7597\u524d\uff0c\u6700\u4f73\u77eb\u6b63\u89c6\u529b\uff08BCVA\uff09\u4ece\u624b\u90e8\u8fd0\u52a8\u523020\/60\u4e0d\u7b49\u3002\u636e\u6089\uff0c\u6709 3 \u540d\u60a3\u8005\u7684\u57fa\u7ebf\u89c6\u529b\u504f\u79bb\u89c6\u529b\u8868\uff0c\u5176\u4e2d 2 \u540d\u60a3\u8005\u7684\u6700\u4f73\u77eb\u6b63\u89c6\u529b\u4e3a\u624b\u90e8\u8fd0\u52a8\u89c6\u529b\uff0c1 \u540d\u60a3\u8005\u7684\u6700\u4f73\u77eb\u6b63\u89c6\u529b\u4e3a\u6570\u624b\u6307\u89c6\u529b\u3002\u8bd5\u9a8c\u4e2d\u67096\u540d\u60a3\u8005\u63a5\u53d7\u4e86\u8f83\u4f4e\u5242\u91cf\u7684NGGT001\uff081.5&#215;1011 vg\/\u773c\uff09\uff0c6\u540d\u60a3\u8005\u63a5\u53d7\u4e86\u8f83\u9ad8\u5242\u91cf\u7684NGGT001\uff083.0&#215;1011 vg\/\u773c\uff09\u3002&#8221;BCD\u662f\u4e00\u79cd\u9057\u4f20\u6027\u89c6\u7f51\u819c\u8425\u517b\u4e0d\u826f\u75c7\uff0c\u5176\u7279\u5f81\u662f\u89c6\u7f51\u819c\u4e0a\u51fa\u73b0\u9ec4\u767d\u8272\u6676\u4f53\u548c\/\u6216\u590d\u6742\u7684\u8102\u8d28\u6c89\u79ef\uff0c\u5e76\u53ef\u80fd\u53d1\u5c55\u6210\u5931\u660e&#8230;&#8230;&#8221;\u3002\u9648\u53ca\u5176\u540c\u4e8b\u5728\u6d77\u62a5\u4e2d\u5199\u9053\uff1a1 &#8220;NGGT001\u5728\u6210\u5e74BCD\u60a3\u8005\u4e2d\u8010\u53d7\u6027\u826f\u597d\uff0c\u7b2c9\u4e2a\u6708\u65f6\u529f\u80fd\u6027\u89c6\u529b\u5f97\u5230\u6539\u5584&#8221;\u3002 \u5355\u51fb\u6b64\u5904\u67e5\u770b\u6709\u5173 2024 ASGCT \u5e74\u4f1a\u7684\u66f4\u591a\u62a5\u9053\u3002 \u4e3b\u8981\u6536\u83b7 \u4e0b\u4e00\u4ee3\u57fa\u56e0\u6cbb\u7597\u516c\u53f8\uff08NGGT\uff09\u751f\u7269\u6280\u672f\u516c\u53f8\u7684 NGGT001 \u662f\u4e00\u79cd\u57fa\u4e8e\u817a\u76f8\u5173\u75c5\u6bd2\uff08AAV\uff09\u8f7d\u4f53\u7684\u57fa\u56e0\u7597\u6cd5\uff0c\u7528\u4e8e\u6cbb\u7597\u6bd4\u57c3\u8482\u6676\u4f53\u6027\u89d2\u819c\u8425\u517b\u4e0d\u826f\u75c7\uff08BCD\uff09\uff0c\u5728\u7814\u7a76\u8005\u53d1\u8d77\u7684\u4e24\u5730\u8bd5\u9a8c\uff08NCT06302608\uff09\u4e2d\uff0c\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u89c6\u529b\u5f97\u5230\u6539\u5584\u3002 \u5728\u63a5\u53d7\u57fa\u56e0\u6cbb\u7597\u4ea7\u54c1\u6cbb\u7597 9 \u4e2a\u6708\u540e\uff0c\u63a5\u53d7\u8be5\u7814\u7a76\u6cbb\u7597\u7684\u53ef\u8bc4\u4f30\u60a3\u8005\u7684\u89c6\u529b\u6bd4\u57fa\u7ebf\u63d0\u9ad8\u4e86 12.8 \u00b1 3.7\uff08\u5e73\u5747\u503c \u00b1 SEM\uff0cn = 11\uff09\u4e2a ETDRS \u5b57\u6bcd\uff0c\u76f8\u5f53\u4e8e\u5728\u65af\u5948\u4f26\u89c6\u529b\u8868\u4e0a\u63d0\u9ad8\u4e86 2-3 \u884c\uff08P = .0026\uff09\u3002 \u4e0e\u7528\u4e8e\u6ce8\u5c04 NGGT001 \u7684\u89c6\u7f51\u819c\u4e0b\u6ce8\u5c04\u7a0b\u5e8f\u6709\u5173\u7684\u4e0d\u826f\u53cd\u5e94\u5305\u62ec\u773c\u7751\u548c\u5de9\u819c\u4e0b\u6c34\u80bf\uff0c\u4f46\u8fd9\u4e9b\u4e0d\u826f\u53cd\u5e94\u7684\u4e25\u91cd\u7a0b\u5ea6\u8f83\u8f7b\uff0c\u5e76\u53ef\u81ea\u884c\u7f13\u89e3\u3002\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u672a\u51fa\u73b0\u773c\u5185\u708e\u75c7\u8ff9\u8c61\u3002\" \/>\n<meta property=\"og:url\" content=\"https:\/\/nggtbio.com\/nggt-\u751f\u7269\u6280\u672f\u516c\u53f8\u7684\u57fa\u56e0\u7597\u6cd5-nggt001-\u80fd\u6539\u5584\u6bd4\u8482\u6c0f\u6676\u4f53\u8425\/\" \/>\n<meta property=\"og:site_name\" content=\"Next Generation Gene Therapeutics\" \/>\n<meta property=\"article:published_time\" content=\"2024-05-09T23:44:54+00:00\" \/>\n<meta name=\"author\" content=\"insightdave\" \/>\n<meta name=\"twitter:card\" content=\"summary_large_image\" \/>\n<meta name=\"twitter:label1\" content=\"Written by\" \/>\n\t<meta name=\"twitter:data1\" 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Therapeutics","og_description":"\u4e0b\u4e00\u4ee3\u57fa\u56e0\u6cbb\u7597\u516c\u53f8\uff08NGGT\uff09\u751f\u7269\u6280\u672f\u516c\u53f8\u7684NGGT001\u662f\u4e00\u79cd\u57fa\u4e8e\u817a\u76f8\u5173\u75c5\u6bd2\uff08AAV\uff09\u8f7d\u4f53\u7684\u57fa\u56e0\u7597\u6cd5\uff0c\u65e8\u5728\u6cbb\u7597\u6bd4\u57c3\u8482\u6676\u4f53\u6027\u89d2\u819c\u8425\u517b\u4e0d\u826f\u75c7\uff08BCD\uff09\u3002\u5728\u7814\u7a76\u8005\u53d1\u8d77\u7684\u4e24\u5730\u8bd5\u9a8c\uff08NCT06302608\uff09\u4e2d\uff0cNGGT001\u6539\u5584\u4e86\u63a5\u53d7\u6cbb\u7597\u60a3\u8005\u7684\u89c6\u529b1\u30021 \u8be5\u7814\u7a76\u7ed3\u679c\u5728 2024 \u5e74 5 \u6708 7 \u65e5\u81f3 10 \u65e5\u4e8e\u9a6c\u91cc\u5170\u5dde\u5df4\u5c14\u7684\u6469\u5e02\u4e3e\u884c\u7684\u7f8e\u56fd\u57fa\u56e0\u4e0e\u7ec6\u80de\u7597\u6cd5\u534f\u4f1a\uff08ASGCT\uff09\u7b2c 27 \u5c4a\u5e74\u4f1a\u4e0a\u4ee5\u6d77\u62a5\u5f62\u5f0f\u516c\u5e03\u3002\u5728\u63a5\u53d7\u57fa\u56e0\u6cbb\u7597\u4ea7\u54c1\u6cbb\u75979\u4e2a\u6708\u540e\uff0c\u63a5\u53d7\u8be5\u7814\u7a76\u6cbb\u7597\u7684\u53ef\u8bc4\u4f30\u60a3\u8005\u7684\u89c6\u529b\u8f83\u57fa\u7ebf\u63d0\u9ad8\u4e8612.8 \u00b1 3.7\uff08\u5e73\u5747\u503c \u00b1 SEM\uff0cn = 11\uff09\u4e2aETDRS\u5b57\u6bcd\uff0c\u76f8\u5f53\u4e8e\u5728\u65af\u5948\u4f26\u89c6\u529b\u8868\u4e0a\u63d0\u9ad8\u4e862-3\u884c\uff08P = .0026\uff09\u3002\u6b64\u5916\uff0c\u5171\u540c\u7b2c\u4e00\u4f5c\u8005\u3001\u53a6\u95e8\u5927\u5b66\u9644\u5c5e\u53a6\u95e8\u773c\u79d1\u4e2d\u5fc3\uff08Xiamen Eye Center of Xiamen University No.989\uff09\u7684\u9648\u79c0\u83ca\u53ca\u5176\u540c\u4e8b\u6307\u51fa\uff0c\u572811\u540d\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u4e2d\uff0c\u67095\u4eba\uff0846%\uff09\u7684\u89c6\u529b\u6bd4\u57fa\u7ebf\u63d0\u9ad8\u4e8615\u4e2aETDRS\u5b57\u6bcd\u4ee5\u4e0a\u3002&#8221;Chen\u53ca\u5176\u540c\u4e8b\u5728\u6d77\u62a5\u6458\u8981\u4e2d\u5199\u9053\uff1a&#8221;BCD\u662f\u7531\u7ec6\u80de\u8272\u7d20P450\uff08CYP\uff09\u5bb6\u65cf4\u4e9a\u5bb6\u65cfV\u6210\u54582\u57fa\u56e0\uff08CYP4V2\uff09\u7a81\u53d8\u5f15\u8d77\u7684\uff0c\u8be5\u57fa\u56e0\u7f16\u7801\u4e00\u79cd\u591a\u4e0d\u9971\u548c\u8102\u80aa\u9178\u7f9f\u5316\u9176\uff0c\u4e3b\u8981\u8868\u8fbe\u4e8e\u89c6\u7f51\u819c\u4e2d\u7684\u89c6\u7f51\u819c\u8272\u7d20\u4e0a\u76ae\u7ec6\u80de\u3002NGGT \u751f\u7269\u6280\u672f\u516c\u53f8\u5f00\u53d1\u4e86\u4e00\u79cd\u57fa\u4e8e rAAV2 \u7684\u8f7d\u4f53 NGGT001\uff0c\u5b83\u8868\u8fbe\u4e86\u7528\u4e8e\u6cbb\u7597 BCD \u7684\u7ecf\u8fc7\u5bc6\u7801\u5b50\u4f18\u5316\u7684\u4eba\u7c7b CYP4V2\u3002\u5728\u5b89\u5168\u6027\u65b9\u9762\uff0cNGGT001\u88ab\u8ba4\u4e3a\u8010\u53d7\u6027\u826f\u597d\u3002\u5176\u4e2d\u4e00\u540d\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u51fa\u73b0\u4e86\u4e24\u4f8b\u773c\u90e8\u6cbb\u7597\u7a81\u53d1\u4e0d\u826f\u4e8b\u4ef6\uff08TEAE\uff09\uff0c\u4e00\u4f8b\u662f\u7ed3\u819c\u6c34\u80bf\uff0c\u4e00\u4f8b\u662f\u773c\u7751\u6c34\u80bf\uff0c\u8fd9\u4e24\u4f8b\u4e0d\u826f\u4e8b\u4ef6\u5747\u57285\u5929\u5185\u7f13\u89e3\uff0c\u88ab\u8ba4\u4e3a\u4e0eNGGT001\u80af\u5b9a\u65e0\u5173\u3002\u5728\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u4e2d\u8fd8\u89c2\u5bdf\u5230\u4e86\u51e0\u4f8b\u975e\u773c\u90e8 TEAEs\u3002\u5176\u4e2d\u5305\u62ec\u4e00\u540d\u60a3\u8005\u7684\u4e24\u4f8b\u4e0a\u547c\u5438\u9053\u611f\u67d3\u3001\u53e6\u4e00\u540d\u60a3\u8005\u7684\u4e00\u4f8b\u5c0f\u817f\u9aa8\u5e94\u529b\u6027\u9aa8\u6298\u4ee5\u53ca\u53e6\u4e00\u540d\u60a3\u8005\u7684\u4e00\u4f8b\u54bd\u708e\u3002\u6240\u6709\u8fd9\u4e9b\u4e0d\u826f\u53cd\u5e94\u90fd\u5728 7 \u5929\u6216\u66f4\u77ed\u65f6\u95f4\u5185\u5f97\u5230\u7f13\u89e3\uff0c\u5e76\u88ab\u8ba4\u4e3a\u4e0e\u57fa\u56e0\u7597\u6cd5\u7edd\u5bf9\u65e0\u5173\u3002Chen\u53ca\u5176\u540c\u4e8b\u8fd8\u6307\u51fa\uff0c\u4e0e\u7528\u4e8e\u6ce8\u5c04NGGT001\u7684\u89c6\u7f51\u819c\u4e0b\u6ce8\u5c04\u7a0b\u5e8f\u6709\u5173\u7684\u4e0d\u826f\u53cd\u5e94\u5305\u62ec\u773c\u7751\u548c\u5de9\u819c\u4e0b\u6c34\u80bf\uff0c\u4f46\u8fd9\u4e9b\u4e0d\u826f\u53cd\u5e94\u7684\u4e25\u91cd\u7a0b\u5ea6\u8f83\u8f7b\uff0c\u5e76\u53ef\u81ea\u884c\u7f13\u89e3\u3002\u4ed6\u4eec\u8fd8\u6307\u51fa\uff0c\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u6ca1\u6709\u773c\u5185\u708e\u75c7\u7684\u8ff9\u8c61\u3002\u8be5\u8bd5\u9a8c\u5171\u5305\u62ec 12 \u540d\u60a3\u8005\uff0c\u5747\u4e3a\u4e9a\u88d4\uff0c\u5e74\u9f84\u5728 30 \u5c81\u81f3 60 \u5c81\u4e4b\u95f4\u3002\u5176\u4e2d\u5305\u62ec 7 \u540d\u7537\u6027\u548c 5 \u540d\u5973\u6027\uff0c\u4ed6\u4eec\u88ab\u786e\u8bca\u4e3a CYP4V2 \u7a81\u53d8\u7684 BCD \u60a3\u8005\u3002\u6cbb\u7597\u524d\uff0c\u6700\u4f73\u77eb\u6b63\u89c6\u529b\uff08BCVA\uff09\u4ece\u624b\u90e8\u8fd0\u52a8\u523020\/60\u4e0d\u7b49\u3002\u636e\u6089\uff0c\u6709 3 \u540d\u60a3\u8005\u7684\u57fa\u7ebf\u89c6\u529b\u504f\u79bb\u89c6\u529b\u8868\uff0c\u5176\u4e2d 2 \u540d\u60a3\u8005\u7684\u6700\u4f73\u77eb\u6b63\u89c6\u529b\u4e3a\u624b\u90e8\u8fd0\u52a8\u89c6\u529b\uff0c1 \u540d\u60a3\u8005\u7684\u6700\u4f73\u77eb\u6b63\u89c6\u529b\u4e3a\u6570\u624b\u6307\u89c6\u529b\u3002\u8bd5\u9a8c\u4e2d\u67096\u540d\u60a3\u8005\u63a5\u53d7\u4e86\u8f83\u4f4e\u5242\u91cf\u7684NGGT001\uff081.5&#215;1011 vg\/\u773c\uff09\uff0c6\u540d\u60a3\u8005\u63a5\u53d7\u4e86\u8f83\u9ad8\u5242\u91cf\u7684NGGT001\uff083.0&#215;1011 vg\/\u773c\uff09\u3002&#8221;BCD\u662f\u4e00\u79cd\u9057\u4f20\u6027\u89c6\u7f51\u819c\u8425\u517b\u4e0d\u826f\u75c7\uff0c\u5176\u7279\u5f81\u662f\u89c6\u7f51\u819c\u4e0a\u51fa\u73b0\u9ec4\u767d\u8272\u6676\u4f53\u548c\/\u6216\u590d\u6742\u7684\u8102\u8d28\u6c89\u79ef\uff0c\u5e76\u53ef\u80fd\u53d1\u5c55\u6210\u5931\u660e&#8230;&#8230;&#8221;\u3002\u9648\u53ca\u5176\u540c\u4e8b\u5728\u6d77\u62a5\u4e2d\u5199\u9053\uff1a1 &#8220;NGGT001\u5728\u6210\u5e74BCD\u60a3\u8005\u4e2d\u8010\u53d7\u6027\u826f\u597d\uff0c\u7b2c9\u4e2a\u6708\u65f6\u529f\u80fd\u6027\u89c6\u529b\u5f97\u5230\u6539\u5584&#8221;\u3002 \u5355\u51fb\u6b64\u5904\u67e5\u770b\u6709\u5173 2024 ASGCT \u5e74\u4f1a\u7684\u66f4\u591a\u62a5\u9053\u3002 \u4e3b\u8981\u6536\u83b7 \u4e0b\u4e00\u4ee3\u57fa\u56e0\u6cbb\u7597\u516c\u53f8\uff08NGGT\uff09\u751f\u7269\u6280\u672f\u516c\u53f8\u7684 NGGT001 \u662f\u4e00\u79cd\u57fa\u4e8e\u817a\u76f8\u5173\u75c5\u6bd2\uff08AAV\uff09\u8f7d\u4f53\u7684\u57fa\u56e0\u7597\u6cd5\uff0c\u7528\u4e8e\u6cbb\u7597\u6bd4\u57c3\u8482\u6676\u4f53\u6027\u89d2\u819c\u8425\u517b\u4e0d\u826f\u75c7\uff08BCD\uff09\uff0c\u5728\u7814\u7a76\u8005\u53d1\u8d77\u7684\u4e24\u5730\u8bd5\u9a8c\uff08NCT06302608\uff09\u4e2d\uff0c\u63a5\u53d7\u6cbb\u7597\u7684\u60a3\u8005\u89c6\u529b\u5f97\u5230\u6539\u5584\u3002 \u5728\u63a5\u53d7\u57fa\u56e0\u6cbb\u7597\u4ea7\u54c1\u6cbb\u7597 9 \u4e2a\u6708\u540e\uff0c\u63a5\u53d7\u8be5\u7814\u7a76\u6cbb\u7597\u7684\u53ef\u8bc4\u4f30\u60a3\u8005\u7684\u89c6\u529b\u6bd4\u57fa\u7ebf\u63d0\u9ad8\u4e86 12.8 \u00b1 3.7\uff08\u5e73\u5747\u503c \u00b1 SEM\uff0cn = 11\uff09\u4e2a ETDRS \u5b57\u6bcd\uff0c\u76f8\u5f53\u4e8e\u5728\u65af\u5948\u4f26\u89c6\u529b\u8868\u4e0a\u63d0\u9ad8\u4e86 2-3 \u884c\uff08P = .0026\uff09\u3002 \u4e0e\u7528\u4e8e\u6ce8\u5c04 NGGT001 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by":"insightdave"},"schema":{"@context":"https:\/\/schema.org","@graph":[{"@type":"WebPage","@id":"https:\/\/nggtbio.com\/nggt-%e7%94%9f%e7%89%a9%e6%8a%80%e6%9c%af%e5%85%ac%e5%8f%b8%e7%9a%84%e5%9f%ba%e5%9b%a0%e7%96%97%e6%b3%95-nggt001-%e8%83%bd%e6%94%b9%e5%96%84%e6%af%94%e8%92%82%e6%b0%8f%e6%99%b6%e4%bd%93%e8%90%a5\/","url":"https:\/\/nggtbio.com\/nggt-%e7%94%9f%e7%89%a9%e6%8a%80%e6%9c%af%e5%85%ac%e5%8f%b8%e7%9a%84%e5%9f%ba%e5%9b%a0%e7%96%97%e6%b3%95-nggt001-%e8%83%bd%e6%94%b9%e5%96%84%e6%af%94%e8%92%82%e6%b0%8f%e6%99%b6%e4%bd%93%e8%90%a5\/","name":"NGGT \u751f\u7269\u6280\u672f\u516c\u53f8\u7684\u57fa\u56e0\u7597\u6cd5 NGGT001 \u80fd\u6539\u5584\u6bd4\u8482\u6c0f\u6676\u4f53\u8425\u517b\u4e0d\u826f\u75c7\u60a3\u8005\u7684\u89c6\u529b - Next Generation Gene 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